Theme: Clinical Trial: Emotions

Clinical Trials: The pioneers and those who come after.

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Clinical Trials: The pioneers and those who come after.

This video is a discussion between two mothers of children with Sanfilippo, both of whom have foundations to drive research. When the gene therapy trial came, one mother’s son was too far progressed in his disorder. The other mother had one child participate in the trial. They discuss the hope contained in the legacy of their children – inspiring and participating in the science as the pioneers that would help those children who come after.