Theme: Clinical Trial: Decision-Making

Clinical Trials: Deciding if this is the right trial – Are you looking for curative or something that mitigates? What if there is a placebo?

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Clinical Trials: Deciding if this is the right trial – Are you looking for curative or something that mitigates? What if there is a placebo?

In this video, a mother of two sons with Duchenne Muscular Dystrophy offers guidance on deciding to participate in a clinical trial. She asks, “what are you looking for- curative treatments vrs mitigating symptoms?”; “What can your children stand – can they tolerate the tests required?”; “Can your family/marriage survive the lifestyle changes you may need to make to participate?”; “What if it is a trial with a placebo arm – can you handle your child getting the placebo?” She encourages asking lots of questions of the trial sponsor, doctors, and the disease community.