Enzyme replacement therapy, Stem Cell Transplant, and Living into the Unknown
Parents of a 4-year old son with Hurler Syndrome talk about their decision to pursue stem cell transplant. “for me it was well Hurlers is a 100 percent fatal, stem cell transplant whatever the mortality rate is lower which is better than a 100 percent mortality rate. We took a shot. The quality of life question is unanswerable so we didn’t ask it.” He’s currently doing really well, but what’s next?